SEARCH HEALTH CONDITIONS BY ALPHABETS
CLN2 Disease
Medications for Neuronal Ceroid Lipofuscinosis
Other names: Vintage Late Infantile Neuronal Ceroid Lipofuscinosis; CLN2 Disease; Late-Infantile Batten Disease; Neuronal Ceroid Lipofuscinosis Type Two
About Neuronal Ceroid Lipofuscinosis: CLN2 disease is an inherited disorder brought on by a mutation in the CLN2 gene which causes a reduced activity of an lysosomal enzyme known as tripeptidyl peptidase 1 (TPP1). The effect of activity of the TPP1 is that proteins and lipid storage in cells and nerves is both abnormal and hence cells cannot function correctly resulting in the development of symptoms. Signs and symptoms of the disease usually begin between 2 yrs old and 4 yrs old with the very first symptom often being hospitalized, progressing to problems with walking and speech, and the disease progresses that the patient gets increasingly dependent on families for most of their daily needs.
Drugs Used to Heal Neuronal Ceroid Lipofuscinosis
The following listing of medications come in some way related to, or used at the treating this condition.
| Drug title | Rx / OTC | Pregnancy | CSA | Alcohol | Reviews | Rating | Popularity |
|---|---|---|---|---|---|---|---|
| Brineura | Rx | N | Add review | 0.0 | |||
Generic name: cerliponase alfa systemic Medicine class: lysosomal enzymes For consumers: dose, side effects For specialists: AHFS DI Monograph, Prescribing Information | |||||||
| cerliponase alfa | Rx | N | Add review | 0.0 | |||
Generic name: cerliponase alfa systemic Brand name: Brineura Medicine class: lysosomal enzymes For consumers: dosage, For professionals: A-Z Drug Facts, AHFS DI Monograph | |||||||
Legend
| Rx | Prescription Only |
|---|---|
| OTC | On The Counter |
| Rx/OTC | Prescription or Over The Counter |
| Away Tag | This drug might not be accepted by the FDA for the treatment of this condition. |
| Pregnancy Category | |
|---|---|
| A | sufficient and well-controlled studies have failed to demonstrate a risk to the fetus in the first trimester of pregnancy (also there isn`t any evidence of risk in later trimesters). |
| B | Animal reproduction studies have failed to demonstrate a risk to the fetus and there are no adequate and well-controlled studies in elderly women. |
| C | Animal research studies have shown a negative effect in the fetus and there are no adequate and well-controlled studies in humans, but potential benefits may warrant used in pregnant women despite potential risks. |
| D | there was positive evidence of human fetal risk based on adverse reaction data from investigational or marketing experience or studies in humans, but potential benefits may justify used in pregnant women despite potential risks. |
| X | Studies in animals or humans have demonstrated fetal abnormalities or there is positive evidence of human fetal risk based on adverse reaction data from investigational or marketing experience, and the risks involved in used in elderly women clearly outweigh potential benefits. |
| N | FDA hasn`t categorized the drug. |
| Controlled Substances Act (CSA) Schedule | |
|---|---|
| N | isn`t at the mercy of the Controlled Substances Act. |
| 1 | includes a high potential for misuse. Has no currently accepted medical use in treatment in the United States. There is just a lack of accepted safety for use under medical supervision. |
| Two | includes a high potential for misuse. Features a currently accepted medical use with severe restrictions or a currently accepted medical use in treatment in the United States. Psychotherapy can cause acute emotional or physical dependency. |
| 3 | Has a potential for abuse less than individuals in programs 1 and 2 2. Features a currently accepted medical use in treatment in the United States. Psychotherapy can lead to moderate or low physical dependence or high psychological dependence. |
| 4 | includes a very low potential for abuse relative to individuals in program 3. It has a currently accepted medical use in treatment in the United States. Psychotherapy can lead to limited physical dependence or psychological dependence relative to individuals in program 3. |
| 5 | includes a very low potential for abuse relative to individuals in program 4. Features a currently accepted medical use in treatment in the United States. Psychotherapy can lead to limited physical dependence or psychological dependence relative to individuals in program 4. |
| Alcohol | |
|---|---|
| X | Interacts with Alcohol. |
Browse Treatment Plans
- A
- B
- C
- D
- E
- F
- G
- H
- I
- J
- K
- L
- M
- N
- O
- P
- Q
- R
- S
- T
- U
- V
- W
- X
- Y
- Z
Further information
Always seek advice from your physician to be sure the information relates to your personal circumstances.
Top USA Pharma Companies
Popular Categories
Easily find an affordable health insurance plan
